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Hereditary Central Nervous System Demyelinating Diseases - 25 Studies Found
Estado | Estudiar |
Recruiting |
Nombre del estudio: Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy Condición: Metachromatic Leukodystrophy Fecha: 2013-01-28 Intervenciones: Genetic: intracerebral administration of AAVrh.10cuARSA |
Active, not recruiting |
Nombre del estudio: Gene Therapy for Metachromatic Leukodystrophy Condición: Lysosomal Storage Disease Fecha: 2012-03-16 Intervenciones: Genetic: Autologous CD34+ stem cells transduced with ARSA encoding lentiviral vector Autologous hematopo |
Completed |
Nombre del estudio: Multicenter Study of HGT-1110 Administered Intrathecally in Children With Metachromatic Leukodystrophy (MLD) Condición: Metachromatic Leukodystrophy (MLD) Fecha: 2011-12-14 Intervenciones: Biological: Recombinant human arylsulfatase A 6 patients treated with HGT-1110 EOW by IT injection |
Completed |
Nombre del estudio: Long-Term Follow-Up Study of Human Stem Cells Transplanted in Subjects With Connatal Pelizaeus-Merzbacher Disease (PMD) Condición:
Fecha: 2011-07-06 Intervenciones: Biological: HuCNS-SC transplant in the lead-in phase Long-term safety follow-up study |
Completed |
Nombre del estudio: Imaging Study of the White Matter Lesions in Children With Metachromatic Leucodystrophy Condición: Late Infantile Metachromatic Leukodystrophy Fecha: 2011-03-09 Intervenciones: Other: High-field MRI (3 Teslas) |
Completed |
Nombre del estudio: Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell Transplantation Condición: Metachromatic Leukodystrophy Fecha: 2011-02-23 Intervenciones: Drug: rhARSA intravenous infusion 100U/kg every other week for 18 months |
Withdrawn |
Nombre del estudio: An Observational Study of Pediatric Subjects With Globoid Cell Leukodystrophy (GLD) Condición: Leukodystrophy, Globoid Cell Fecha: 2010-03-24 |
Completed |
Nombre del estudio: Study of Human Central Nervous System (CNS) Stem Cells Transplantation in Pelizaeus-Merzbacher Disease (PMD) Subjects Condición: Pelizaeus-Merzbacher Disease Fecha: 2009-10-28 Intervenciones: Biological: HuCNS-SC cells intracerebral transplantation |
Completed |
Nombre del estudio: The Natural History of Infantile Globoid Cell Leukodystrophy Condición: Infantile Globoid Cell Leukodystrophy Fecha: 2009-09-23 |
Active, not recruiting |
Nombre del estudio: Diffusion Tensor Imaging (DTI) in Infants With Krabbe Disease Condición: Krabbe Disease Fecha: 2008-11-07 |